Every year, over a million babies are born worldwide with a hereditary disease. Many are serious, some fatal. For most of history, doctors could only treat symptoms. Then researchers began to target root causes, but the quest has been long, difficult, and punctuated by tragedy. Now an elite cadre of pioneers—call them gene doctors—is starting to win battles.

Through intimate stories of families whose lives are being transformed, The Gene Doctors takes viewers to the front lines of a medical revolution. With early successes and new treatments appearing on the horizon, families battling genetic diseases have never had such good reasons for hope.